Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials

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Offline Pratik

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Re: Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials
« Reply #45 on: September 20, 2012, 10:11:01 AM »
Recruitment in the US has gone slow, possibly because some misinformation about the goal of the trial. The goal is to cure patients. If the procedure works as expected, patients will be cured.
Is there any risk? Like if it fails, nothing will happen to the patient right unlike BMT?

Regards.
Every child is special.

Andy , sharmin,

is thereul   any report of successful gene therapy?

we are all waiting for good thing.

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Offline Andy Battaglia

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The latest email from Pat G that came a couple days ago said that two patients have been accepted for the trial and the first will be dosed in December. Results will be known after 40 days.

Patients in the US: Patients are still being accepted for trials. If this works as expected, patients will be cured.
Andy

All we are saying is give thals a chance.

Thanks Andy, This is good news.

It is my understanding that total 10 patients are to be recruited at inital stage (Phase 1).
Regards.

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Offline Andy Battaglia

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They definitely want more patients, but things were slowed by some misinformation that was put out by one of the doctors who is no longer allowed to speak publicly about the trial. Hopefully, we will see more patients apply.
Andy

All we are saying is give thals a chance.

Re: Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials
« Reply #50 on: November 14, 2012, 05:59:09 AM »
Update: Beta-Thalassemia Treatment Approved For FDA's Clinical Phase I Trials - http://www.csrwire.com/press_releases/34862-Beta-Thalassemia-Treatment-Approved-For-FDA-s-Clinical-Phase-I-Trials

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Offline Andy Battaglia

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Re: Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials
« Reply #51 on: November 14, 2012, 06:14:10 AM »
We can expect the first patient to start soon, possibly in the next two weeks, with results known after about 40 days.
Andy

All we are saying is give thals a chance.

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Offline Pratik

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Re: Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials
« Reply #52 on: November 14, 2012, 09:08:41 AM »
Interesting. Let's pray for the best.

-P.
Every child is special.

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Offline Sharmin

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Re: Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials
« Reply #53 on: November 14, 2012, 04:51:34 PM »
Praying....

Sharmin

Re: Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials
« Reply #54 on: November 20, 2012, 05:19:51 PM »
Praying for the success...
Regards.

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Offline Sharmin

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Re: Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials
« Reply #55 on: November 24, 2012, 07:27:30 PM »
Is anyone aware of whether the trials commenced this week?  Hopefully the first patient has been infused...

Sharmin

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Offline Parin

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Re: Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials
« Reply #56 on: November 25, 2012, 04:59:55 PM »
Yes, Pat said it will be on 23 Nov...I am also waiting for...There was a Thal confer in Delhi where Pat and Dr. Saleden was present....I guess may they have disclosed...if anyone attended the conf ...Please shaare the update..

Thanks You.

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Offline Andy Battaglia

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Re: Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials
« Reply #57 on: November 26, 2012, 12:56:14 AM »
The first report from the Delhi conference is that Dr Sadelain announced that three patients have started!

 :yaaaaaay
Andy

All we are saying is give thals a chance.

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Offline Sharmin

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Re: Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials
« Reply #58 on: November 26, 2012, 01:26:32 AM »
Tears of joy - I'm so happy for every thalassemia patient today. 

Hoping for good news in 40 days...
Sharmin

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Offline Pratik

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Re: Recruiting patient for Thalgen Finally! Good News about Gene Therapy Trials
« Reply #59 on: November 26, 2012, 01:43:18 PM »
The first report from the Delhi conference is that Dr Sadelain announced that three patients have started!

 :yaaaaaay
That is worth to cry.

I really really hope that this surpasses all the boundless limits thalassemia majors had until now.

Praying so hard.

Also are all 3 Indian patients and their treatment is undergoing in India or USA?

Keep us updated Andy.

-P.
Every child is special.

 

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