• Welcome, Guest. Please login or register.
    November 11, 2019, 01:27:19 PM

  • Login with username, password and session length

Sajid's dove

Tell everyone they can now find this site by typing this into their browser:


Click to visit us on Facebook

If you have any problems registering or signing in, please send an email to: andythalpal@yahoo.com
Please do not send questions about thalassemia to this address.


Thalassemia Patients and Friends and thalpal Ā© A. Battaglia 2019

55155 Posts in 5879 Topics by 6154 Members
Latest Member: Catking

We love you, Lisa.
May you Rest in Peace,
knowing that your legacy lives on,
right here, and through all of us.
You're forever in our hearts.
« previous next »
Pages: 1 Go Down Print
Author Topic: REBLOZYL (Luspatercept) Approved by FDA  (Read 45 times)
Andy Battaglia
Supreme Member
Offline Offline

Location: In my heart, Maldives

Gender: Male
Posts: 8604

Will thal rule you or will you rule thal?

« on: November 08, 2019, 03:40:51 PM »

Great news today! The new drug, REBLOZYL (Luspatercept) has been approved by the FDA today.


REBLOZYL is the first and only FDA-approved erythroid maturation agent, representing a new class of therapy which works by regulating late-stage red blood cell maturation to help patients reduce their RBC transfusion burden.
REBLOZYL is anticipated to be available [in the US] 1 week following the FDA approval.

At this point, I do not know when it will become available outside the US, but I will try to inform once I know more.


All we are saying is give thals a chance.
New Member
Offline Offline

Posts: 18

« Reply #1 on: Yesterday at 01:06:52 PM »

Great news! First Gene therapy approval and now this. This definatly is a big step forward. Let's hope everyone is able to reap benefits of these new modes of treatments as early as possible. Although this may not get us totally off transfusions, but there is a silver lining:)
New Member
Offline Offline

Posts: 22

« Reply #2 on: Today at 08:16:17 AM »

Great News!!

Do we know if only Adults or Kids also can be benefited once it is available?
Senior Member
Offline Offline

Posts: 294

« Reply #3 on: Today at 08:47:15 AM »

Thank you for this great news Andy!
Please can you help me to understand how exactly it works, although you have highlighted it.
I thought the Hb weakens when blood cells mature. Sorry mind fog. Will it be in medicine form?

Thank you and sorry just can't seem to think straight at the moment.
Pages: 1 Go Up Print 
« previous next »
Jump to:  

Powered by MySQL Powered by PHP Powered by SMF 1.1.21 | SMF © 2015, Simple Machines Valid XHTML 1.0! Valid CSS!