Discussion Forums > Working Towards a Cure
Gene Transfer Therapy Stage 1 Clinical Trials at Sloan Kettering
Andy Battaglia:
It is far too early to give any estimates on when this will be available outside of trials. Years of monitoring will be needed to see if any long term side effects develop and if the gene will continue to produce beta globin as years go by. Trials will remain the only way to take advantage of this for the time being.
catchR:
Hello Andy,
Its July'14 now and do we have any feelers / tentative dates on when Dr. Sadelain and team would publish their work on thalgen trails??
Also, do we know anything from Alicia Somma (part of trails) on how well things have worked out?
fingers crossed....hoping for the very best!!
Andy Battaglia:
I just got off the phone with Pat Girondi. They have a meeting come up soon and we should be able to get more information after that. He did tell me that the first two patients who started at SK have a greatly reduced transfusion regimen now, and a third patient in his 40's has had some gene expression but less than is needed. It may be that a higher dose is needed in older patients. Keep in mind that these are all beta thal majors and not HbE beta thals, as the early patients that Bluebird has treated are.
Canadian_Family:
Hi Andy,
Thanks for the update. I think its about time for SK to announce the results. Looking forward to more detailed version of results.
Bostonian_04:
Andy, Thanks for the update. Hoping for more info of the results and next steps from SK...
Navigation
[0] Message Index
[#] Next page
[*] Previous page
Go to full version