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Gene Therapy Update From The Philadelphia Conference.

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Andy Battaglia:
Dr Michel Sadelain was a surprise speaker at the Philly conference, and as always, it as a pleasure to meet him. David Davidson from Bluebird also spoke on his company's upcoming trials and future endeavors. I must admit, I was impressed by both speakers.

I want to give an update on something we have all been waiting for. The future for gene therapy is looking more promising than ever. The French patient is still well and transfusion independent. The trials currently being run at Sloan Kettering are still very early in the going, but the results are outpacing those of the French patient at this point in the trial, even though a low intensity chemo program was utilized. It was expected that the results would come at a slower pace than what has been seen so far. It is early on, and we should remember that results for the French patient were not released until 3 years into the trial.
I will also mention that the other company that will be running trials, Bluebird, will be recruiting patients internationally and will be paying expenses to the US for the trial. I was impressed by both gene therapy presentations. Over the next 25 years, we will be seeing a revolution in the treatment of genetic disorders.

Dharmesh:
It's A WOOOOOOOOOOW :biggrin :yahoo

But 25 yrs is not much long??

I am expecting it to be 10 yrs

ANI:
I just fail to understand that if the french patient is doin well after 3 years, what is the harm of calling it a success. S/ He must be undergoing various test and is that not enough to understand his condition.
Also, one more thought cramps in my mind that instead of different companies working in isolated manner, can there not be a synchronized effeort t make this success. We are ar certain strage and many experimentation has been done of diff paatients. Its the matter of consolidating the journey and proceeed from there.
Ha. I feel the US governemnt has many other jobs and may be it is just another problem for them.
We as parnet and patients are waiting and waiting. may be another 10-15 more years.

Sushil:
I dont know how i should react, but to wait for this treatment for another 25 years is not what i was expecting. Anyhow we do not have any other option as this is the only ray of hope.

Regards
Sushil Thakur

JV:
I think Andy was saying 25 years for the treatment of OTHER genetic disorders not thal

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