Discussion Forums > Working Towards a Cure
Bluebird Bio Releases Data on Current Gene Therapy Trials
Andy Battaglia:
Bluebird today released the full data on their first two patients in their current gene therapy trials. Both are responding well and have not had a transfusion since the second week of the trials. The full pdf is attached to this post. If you have questions, please ask them, as I will be able to talk to Bluebird again in the coming weeks to ask any follow up questions you may have.
This is a very exciting time. The early results are quite good and show good expression of the HbB-A-T87Q, which is the adult hemoglobin being produced by their process.
I want to thank Bluebird Bio for being kind enough to spend some time talking to me and answering and explaining this process which is very important to all of you. Those attending the CAF conference this weekend will see presentations from Bluebird and also from Sloan Kettering where a separate trial is taking place.
JV:
This is great Andy, thank you for all your efforts
Bostonian_04:
This is great news. Thank you Andy for the attached presentation. They saw positive outcome for β0/βE -thalassemia major...Will this be seen in β0/β0 or other mutations as well? Will the treatment is less harsh than BMT?
Parin:
Thanks Andy...for sharing the great news..hope soon it will available to all....
catchR:
This is really amazing news, thank you Andy for sharing the updates!! Awaiting results from Dr. Sadelain on their trails...
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