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Bluebird Bio Releases Data on Current Gene Therapy Trials

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princessaurora:
Good day my daughter Aurora was recently diagnosed as being beta thalesssemia
 intermediate we live in the Caribbean as a parent I would like to know how I can get my daughter cured

Andy Battaglia:
Right now, the only approved cure is a bone marrow transplant. This is usually only done if the patient is transfusion dependent. It should only be a few years before gene therapy will be approved and that will also definitely cure intermedia patients. Does the child take blood transfusions?

Parin:
bluebird bio Q3 Update

http://investor.bluebirdbio.com/static-files/37fe317c-5c01-43af-9c1d-2decb9d3800d

Andy Battaglia:
We should see a new update after next week's presentation at ASH.

Parin:
First presentation of data from patients with a β0/β0 genotype and a pediatric patient treated with LentiGlobin in Phase 3 Northstar-3 study both have stopped chronic blood transfusions

10 of 11 patients with non-β0/β0 genotypes and more than three months follow-up have stopped chronic transfusions in Phase 3 Northstar-2 study

Indicators of poor red blood cell production appear corrected in exploratory analysis of bone marrow following treatment with LentiGlobin


http://investor.bluebirdbio.com/news-releases/news-release-details/bluebird-bio-presents-new-data-lentiglobin-gene-therapy

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