Discussion Forums > Working Towards a Cure

Bluebird bio Webinar 12/10/15

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Canadian_Family:
Well Said Andy.

All great inventions took several shots to perfect them. Read history, tell me one invention which was invented in first try...........

Andy Battaglia:
I've actually been quite surprised at how well the first efforts at gene therapy have gone. Many said it had no hope at all. I truly believe that we will eventually see gene therapy understood well enough to cure a hoist of disorders.

Sharmin:
I agree Andy and Canadian Family, the immense progress we have seen in the last few years is beyond belief.  Even a hemoglobin of 10 would be great for beta zeros.  Heck, my grandma lived to be 90 with a hemoglobin of 10 - and she did not stop walking and working until her last breath.  Of course even higher hemoglobins are likely possible and would be ideal.  We also need to realize how gene therapy is eliminating most of the risks of BMT - bmt is associated with higher mortality risks and gvhd.  I am grateful for the progress thus far and hope that more progress is made soon. 

Thank you again Andy.   

Sharmin

catchR:
Thanks Andy for sharing this information!! we have lot of hope pinned on success of gene therapy and strongly believe that bluebird will make it reality in coming years...

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