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EGT - company working on cures for Orphan Diseases

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Bostonian_04:
Hi all,

My wife and I came across a website for Errant Gene Therapeutics, LLC (based in Chicago) that works towards development of treatments for orphan diseases. One of their areas of research is gene therapy for thalassemia and one of their lead product candidates is Thalagen, that targets Thalassemia.

The relevant webpage for the company is:

http://www.errantgene.com/About_Errant_Gene-Company-Profile.shtml

============================
Errant Gene Therapeutics, LLC™ was established in October 2003 by Patrick Girondi and Norbert L. Wiech, Ph.D. to develop treatments for life-threatening diseases, in particular those recognized as rare disorders or orphan diseases.


EGT’s primary strategy is to address the unmet medical needs of patients with orphan diseases through the development of its technology and treatments. In addition, the company maintains a constant search for new therapeutic advancements that have the potential to be developed into future treatments. The company's strong intellectual property position is the result of world-wide exclusive licensing agreements from prominent academic laboratories and the acquisition of proprietary technology.

The EGT lead product candidates, Thalagen and CG 1521, target the treatment of the blood disorder thalassemia and refractory prostate cancer, respectively. These products are based on pharmacological technology which corrects the errant gene expression causing each disorder. EGT is currently developing two technologies which can be rapidly introduced into human clinical trials, studied and made available to patients. Thalagen is a treatment for thalassemia based on the technology of gene therapy; CG 1521 is an inhibitor of histone deacetylase and represents a new treatment paradigm for therapy resistant prostate cancer.


Additional product candidates in development target pulmonary and neurodegenerative disorders.
===========================

Some more info on their product pipelines and research are available at:

http://www.errantgene.com/Product_Pipeline-Overview.shtml
http://www.errantgene.com/Product_Pipeline-Thalagen.shtml

Some information on Patrick Girondi is available on his webpage at:

http://www.patgirondi.com/For_my_Friends/about.php

What do you guys think about this? Has anyone else heard about them - maybe CAF or any other thalassemia research organization in the US?

Regards,

Bostonian

Manal:
Hello Bostonian

I emailed them last July and they said that Thalagene is not yet available and that they are starting the human clinical trails and they adviced me to keep checking their site for any further develpment.

Hope this helps
Manal

Christine Mary:
Hi Bostonian and Manal,

All I know is, I am keeping my fingers triple crossed, and I am very excited about the potential of a cure SOON!!!
 :clap :yahoo :cheer :boogie :heartpink :thumbsup :love :party :stars :goodluck :sorrow :high5 :wootwoot :grin :pray :pray :pray :pray :pray :pray :pray :pray :pray :pray :pray :pray :pray :pray :pray

Narendra:
Hello Team,

Here is an update on the Approval for RAC in June 2007

From:- http://www.errantgene.com/Product_Pipeline-Thalagen.shtml


--- Quote ---EGT has secured approval from the The Recombinant DNA Advisory Committee (RAC) to proceed with gene therapy clinical trials for Thalagen™.
--- End quote ---


Hope the trials starts soon and we get to a cure in the next few years.

Canadian_Family:
Very Interesting, The link from their website shows they are begining phase 1 soon.

http://www.errantgene.com/Product_Pipeline-Overview.shtml

Regards




 

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