Thalassemia Patients and Friends

Discussion Forums => Working Towards a Cure => Topic started by: zahra on February 15, 2012, 04:30:28 PM

Title: Gene therapy
Post by: zahra on February 15, 2012, 04:30:28 PM

Hi everybody,
My sons doctor mentioned that gene therapy for thalassemia has progressed to the human trial stage in the US and UK. This is not the same as the French Hb E/ b thal trial earlier. I haven't been able to find anything on this online. Does anyone have any info on these new trials?
Zahra

Title: Re: Gene therapy
Post by: Sharmin on February 15, 2012, 11:29:32 PM

Hi Zahra,

Your son's doctor may be referring to the errant gene/sloan kettering trials, headed by Michel Sadelaine which are poised to begin once some issues are ironed out.  Hopefully we will have more information next month. 

Sharmin