Thalassemia Patients and Friends

Discussion Forums => Curing Thalassemia. Bone Marrow & Cord Blood Transplant => Topic started by: JV on January 12, 2013, 12:30:44 AM

Title: Article from Cooley's Anemia website
Post by: JV on January 12, 2013, 12:30:44 AM

http://www.cooleysanemia.org/index.php?option=com_content&view=article&id=595%3Aus-based-gene-therapy-study-begins-treating-participants&catid=1%3Alatest-news&Itemid=1

Title: Re: Article from Cooley's Anemia website
Post by: Andy Battaglia on January 12, 2013, 01:35:19 AM

We are hoping to hear the first report by late next week.

Title: Re: Article from Cooley's Anemia website
Post by: Pratik on January 12, 2013, 05:33:12 AM

I was just about to post this as I too received an email. :)

Very happy.

-P.

Title: Re: Article from Cooley's Anemia website
Post by: Sharmin on January 12, 2013, 09:31:07 PM

It is so great that these trials have finally started - I am praying for a great outcome. 

Thank you for keeping our faith all of these years Andy - you have always said that Dr. Saidelaine's method will be successful one day - I hope that time has come....

Sharmin

Title: Re: Article from Cooley's Anemia website
Post by: Andy Battaglia on January 13, 2013, 03:33:42 AM

I think the only question is if the chemo regimen is intense enough. I don't think there's any question about the gene therapy itself working. This group feels that we have to try with a low intensity regimen right from the start, and I agree. Why cause patients more harm with chemo than necessary? Since the vector for the first gene therapy trial in Europe came from Thalagen, and this vector is 10 times stronger than that one, I have confidence that it will work, as long as the chemo has done its job.