Thalassemia Patients and Friends

Discussion Forums => General Chatter => Topic started by: mumtaz on August 13, 2007, 04:28:50 PM

Title: what are the News regarding Gene tharapy in thal patients?
Post by: mumtaz on August 13, 2007, 04:28:50 PM

Hello friends
is there any new regarding gene tharapy in thal patients? is is going in right direction? and how much chances r there that it will be sucessful therapy?
As i was intrested in BMT for my son, but the cost is very high and also i read that BMT having a lot of complications.

thx for ur reply

Title: Re: what are the News regarding Gene tharapy in thal patients?
Post by: Andy Battaglia on August 13, 2007, 04:55:37 PM

Gene therapy trials for thalassemia have now been approved in the US and it is hoped that two trials will begin by the middle of 2008, provided that the necessary funding can be arranged.

We have had some recent posts on this topic at

http://www.thalassemiapatientsandfriends.com/index.php?topic=713.0
http://www.thalassemiapatientsandfriends.com/index.php?topic=1114.0
http://www.thalassemiapatientsandfriends.com/index.php?topic=1115.0

My opinion is that gene therapy presents the best possibility for a safe cure for thalassemia but it will take years of trials before it can be made available for patients.