Thalassemia Patients and Friends

Discussion Forums => Working Towards a Cure => Topic started by: nwalsh528 on October 28, 2012, 10:38:02 PM

Title: Gene Transfer Therapy Clinical Trials at Sloan Kettering (stage 1)
Post by: nwalsh528 on October 28, 2012, 10:38:02 PM

I was so encouraged to read this. For those of us who would not attempt a BMT (with or without a perfect sibling match), this (if successful) would truly be a "cure" without risking host v. graft. The patient's OWN stem cells would be used. Hoping the vector being used in these clinical trials will have better results than previous one(s) (as they caused cancer...)
http://www.mskcc.org/blog/launch-stem-cell-therapy-trial-offers-hope-patients-inherited-blood-disorder
Nicole

Title: Re: Gene Transfer Therapy Clinical Trials at Sloan Kettering (stage 1)
Post by: Pratik on October 29, 2012, 06:26:35 AM

This is very amazing, I would be so glad to hear about the results when more patients are recruited.