Bluebird Bio Releases Data on Current Gene Therapy Trials

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Re: Bluebird Bio Releases Data on Current Gene Therapy Trials
« Reply #180 on: October 27, 2018, 03:54:49 PM »
Good day my daughter Aurora was recently diagnosed as being beta thalesssemia
 intermediate we live in the Caribbean as a parent I would like to know how I can get my daughter cured

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Offline Andy Battaglia

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Re: Bluebird Bio Releases Data on Current Gene Therapy Trials
« Reply #181 on: November 03, 2018, 06:56:46 PM »
Right now, the only approved cure is a bone marrow transplant. This is usually only done if the patient is transfusion dependent. It should only be a few years before gene therapy will be approved and that will also definitely cure intermedia patients. Does the child take blood transfusions?
Andy

All we are saying is give thals a chance.


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Offline Andy Battaglia

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Re: Bluebird Bio Releases Data on Current Gene Therapy Trials
« Reply #183 on: November 29, 2018, 09:21:38 PM »
We should see a new update after next week's presentation at ASH.
Andy

All we are saying is give thals a chance.

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Offline Parin

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Re: Bluebird Bio Releases Data on Current Gene Therapy Trials
« Reply #184 on: December 04, 2018, 05:42:19 AM »
First presentation of data from patients with a β0/β0 genotype and a pediatric patient treated with LentiGlobin in Phase 3 Northstar-3 study both have stopped chronic blood transfusions

10 of 11 patients with non-β0/β0 genotypes and more than three months follow-up have stopped chronic transfusions in Phase 3 Northstar-2 study

Indicators of poor red blood cell production appear corrected in exploratory analysis of bone marrow following treatment with LentiGlobin


http://investor.bluebirdbio.com/news-releases/news-release-details/bluebird-bio-presents-new-data-lentiglobin-gene-therapy

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Offline Andy Battaglia

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Re: Bluebird Bio Releases Data on Current Gene Therapy Trials
« Reply #185 on: December 04, 2018, 03:29:07 PM »
The results are spectacular. After much negativity from some quarters about the earlier results from the non beta zero trials, we have fantastic news. Yes, only 3 patients have been started so far, but all 3 beta zero patients are transfusion free. The new protocol is working.
Andy

All we are saying is give thals a chance.

Re: Bluebird Bio Releases Data on Current Gene Therapy Trials
« Reply #186 on: December 04, 2018, 08:38:02 PM »
Great news .
Dear Andy when can be this treatment available in market ?

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Offline Andy Battaglia

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Re: Bluebird Bio Releases Data on Current Gene Therapy Trials
« Reply #187 on: December 04, 2018, 11:49:50 PM »
bluebird bio has begun the approval process in Europe. It's only a guess, but I would hope that within two years, we will see the first approval for gene therapy for thalassemia.
Andy

All we are saying is give thals a chance.

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Offline Parin

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Re: Bluebird Bio Releases Data on Current Gene Therapy Trials
« Reply #188 on: December 05, 2018, 07:00:06 AM »
Thanks Andy

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Offline Parin

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Re: Bluebird Bio Releases Data on Current Gene Therapy Trials
« Reply #189 on: March 31, 2019, 06:13:30 AM »
bluebird bio Receives Positive Opinion from CHMP for ZYNTEGLO™ (autologous CD34+ cells encoding βA-T87Q-globin gene) Gene Therapy for Patients 12 Years and Older with Transfusion-Dependent β-Thalassemia (TDT) Who Do Not Have β0/β0 Genotype

http://investor.bluebirdbio.com/news-releases/news-release-details/bluebird-bio-receives-positive-opinion-chmp-zynteglotm

Re: Bluebird Bio Releases Data on Current Gene Therapy Trials
« Reply #190 on: April 02, 2019, 11:30:06 AM »
Finally....some exciting news!!


is gene therapy from bluebird going to cost 2.12 mUSD??
« Last Edit: April 17, 2019, 05:21:38 PM by catchR »

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Offline Parin

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Re: Bluebird Bio Releases Data on Current Gene Therapy Trials
« Reply #191 on: April 03, 2019, 02:08:48 AM »
2.12 m USD?   :rolleyes :rolleyes

 

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