Discussion Forums > Working Towards a Cure
Bluebird Bio Releases Data on Current Gene Therapy Trials
Sharmin:
That is all very concerning. Things are not moving at SK at all. Most of our cards are on BB at this time. With the momentum these two groups started off last year - it is very surprising that more exciting news is not coming out and there is no sign of new patients being treated by either group.
The last BB update in November stated that the first two patients continue to be transfusion free, expressing high rates of the new hemoglobin.
Praying for the best news from both of these groups.
Very disappointing that what is a life line for some of us - is a money making scheme for some :(
JV:
Sharmin, that was very well put. We have been all in since day one and for a major organization like SK to not be more proactive is extremely disappointing. Hoping for Bluebird to run with it now...
Bostonian_04:
Latest from Bluebird....
Bluebird posts more promising results for its rare disease therapy
December 8, 2014
http://www.fiercebiotech.com/press-releases/bluebird-bio-announces-data-demonstrating-first-four-patients-thalassemia-m
Andy Battaglia:
These results include the first that Bluebird has done using thalassemia major patients. The early results are quite impressive. We will be eagerly waiting for the results on the one sickle cell patient that has started.
It is still quite early on, and hopefully there will be no serious issues develop down the road, but we now know with certainty that gene therapy does work. I will not hesitate to tell patients to take part in trials if eligible. It may be the only way many patients will ever be able to afford it.
Sharmin:
Bostonian,
Thank you soooo much for posting this! Such great news! Praying that it provides a solution for everyone suffering from thalassemia or sickle cell anemia!
Sharmin
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